Doctors treat baby's genetic disorder with CRISPR

Doctors have successfully used CRISPR gene-editing to create a customized treatment for a baby with a rare, life-threatening genetic disorder, marking a medical first. The therapy appears to have partially reversed the baby's condition. The treatment, tailored to the baby's specific genetic mutation, involved three infusions of gene-editing tools. These tools targeted and corrected a defect in the baby's liver, reducing the risk of brain damage and potentially death. The baby is showing positive signs. This breakthrough opens doors for personalized medicine, particularly for rare diseases. Researchers hope this approach will lead to faster and more affordable gene-editing treatments, potentially transforming the treatment of numerous genetic conditions.