Harvard scientists use gene editing to treat rare brain disease in mice

Harvard scientists have used gene-editing technology to successfully treat a rare brain disease in lab mice, offering hope for a cure. The technique, developed by David Liu's lab, corrected genetic flaws causing alternating hemiplegia of childhood (AHC) in mice, leading to fewer seizures and improved cognition. This breakthrough, supported by the Frost family's advocacy, could pave the way for treating other genetic neurological disorders.