Gene therapy slows Huntington's disease progression by 75 percent in trial

singularityhub.com

A gene therapy trial showed a 75 percent slowing of Huntington's disease progression over three years. The therapy, AMT-130, involves a single microRNA injection into the brain, improving motor control and cognitive function in patients. While preliminary and with a small sample size, the results offer significant hope for a disease with no current treatments.


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