First boy receives gene therapy for rare Hunter's disease in Manchester, UK

dn.se (Swedish)

A three-year-old boy is the first globally to receive gene therapy for the rare Hunter's disease, showing promising results with normal development. The boy, Oliver Chu, underwent the experimental treatment in Manchester, UK, where his own cells were modified to produce a crucial missing enzyme. This therapy aims to halt the progressive damage caused by the genetic disorder. The study involves five boys, and if successful, researchers hope to gain approval for the treatment to help more children affected by this rare condition.


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